Weekly Spotlight - 14.11.24

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In the News

Capsida's Gene Therapy Shows Promise for Friedreich's Ataxia Treatment

Capsida Biotherapeutics has unveiled promising preclinical data for CAP-004, a gene therapy targeting Friedreich's ataxia. This therapy shows potential in treating neurological, cardiac, and sensory symptoms. CAP-004's safety profile is favourable, with minimal off-target effects. The therapy will be presented at the International Congress for Ataxia Research.

Proactive Planning for Medical Appointments Eases Stressful Experiences

Elizabeth Hamilton shares her proactive approach to scheduling medical appointments for her daughter, Amelia, who has Friedreich's ataxia. By preparing thoroughly and requesting specific support, such as a child life specialist and IV ultrasound team, she aims to reduce trauma and improve Amelia's hospital experiences.

Gardening with FA: Embracing Nature's Healing Power

Spending time in nature significantly benefits those with Friedreich's ataxia (FA), enhancing mental health and overall wellness. Jean Walsh shares her personal experience, highlighting gardening as a therapeutic activity. She offers practical tips for gardening with FA, emphasising the restorative power of nature on mood and fatigue.

Male Mice Show More Severe Heart Issues in Friedreich's Ataxia Study

Male mice with Friedreich's ataxia exhibit more severe heart issues and shorter lifespans than females, highlighting sex differences in disease impact. The study suggests testosterone's role in heart health, urging further hormone research. This model aids in developing treatments, offering hope for better understanding and management of the condition.